Case Studies
Alkaptonuria, a rare cause for low back pain
Vikram
Muralidhar Haridas*
Author Affiliation
Arthritis Super Speciality Center, Hubli,
India
* Correspondence: Dr.Vikram Muralidhar Haridas,
IJRCI. 2013;1(1):CS5
Received: 6 May 2013, Accepted: 26 July 2013, Published: 2
September 2013
© IJRCI
Abstract
Alkaptonuria is a very rare disease that can cause premature degenerative arthritis of the spine and peripheral large joints. I present here a case of middle-aged woman who developed low back pain secondary to alkaptonuria.
Case report
A 45-year-old female
presented with a history of low back pain since 10 years. She had difficulty in
bending, restriction in back movements, and scoliosis. She was also
experiencing early morning stiffness, which improved with activity, and pain on
both the knee joints without swelling. The patient had a family history of
similar complaints and the affected family members also demonstrated back pain.
She had also reported the occurrence of urine turning black after some time
(Fig 1). Physical examination demonstrated the blackish discoloration of ears
as well as the pigmentation of sclera (Fig 2). Examination of the spine showed kyphoscoliosis with normal spinal mobility. Anteroposterior X-ray of the spine showed intervertebral disc calcification with normal sacroiliac
joint (Fig 3).
Fig 1: Change in urine
color when exposed to air
Fig 2: Pigmentation of the ear and sclera
Fig 3: X-ray showing pelvis with normal
sacroiliac joint and lateral thoracolumbar spine with
intervertebral disc calcification
Discussion
Alkaptonuria, a rare defect with autosomal recessive inheritance, is caused by the abnormal tyrosine catabolism due to the deficiency in homogentisic acid oxidase. The enzyme catalyzes the catabolism of homogentisic acid to molecules that can be used in Krebs cycle. Deposition of homogentisic acid produces gray to blue pigment in the tissues. It can cause pigment deposition in the connective tissue of eye, ear, cartilage, and cardiac valves. Generally, the disease will be asymptomatic, but may appear in the middle age due to early degenerative arthritis involving lower spine, and shoulder and hip joints requiring early joint replacement. The current incidence of the disease is estimated to be 1 in 250,000 -1,000,000 live births.1
Alkaptanuria should be suspected in patients with the following clinical triad:
1. Degenerative arthritis (premature) i.e. in young patients of <45 yrs.
2. Abnormal pigmentation of connective tissues in eye, ear, and cardiac valves.
3. Urine turning blue-black on standing (due to alkalinization).
Since homogentisic
acid is absent in the blood plasma and urine of healthy subjects, both of them
can be used for the disease diagnosis. In alkaptonuria
patients, the average levels of homogentisic acid
noted in the plasma and urine are 6.6 micrograms/ml and 3.12 mmol/mmol of creatinine
respectively.1 Confirmatory tests for diagnosis are paper
chromatography and thin layer chromatography.
Characteristic radiological findings include
vertebral disc calcification, chondrocalcinosis, and
osteoarthritis of multiple joints (especially spine) at young age.
Since most of the young patients with alkaptonuria present with low back pain, it can mimic
ankylosing spondylitis. Generally, the disease could be suspected in young patients
with low back pain and X-ray showing intervertebral disc calcification with
normal sacroiliac joint. They can also have premature osteoarthritis of knee or
other major joints. A detailed history and examination may reveal black
staining of the undergarment, change in the urine color on longstanding,
pigmentation of sclera, and grayish hue discoloration of the ears. First-degree
relatives may have symptomatic scleral pigmentation
and ear discoloration before they develop any joint manifestation (as many are
unaware of the urine color change or staining of clothes).
No treatment modality has been unequivocally proven to reduce the complications of alkaptonuria. Commonly advocated treatment strategies include large doses of ascorbic acid (vitamin C) and dietary restriction of tyrosine and phenylalanine. Although, dietary restriction may be effective in children, it has not shown any benefits in adults.1
Competing interests
The
author declares that he has no competing interests.
References
1. Grier
Phornphutkul C, Introne WJ,
Perry MB, Bernardini I, Murphey
MD, Fitzpatrick DL, et al. Natural History of Alkaptonuria.
New England Journal of Medicine. 2002;347(26):2111–21.